Small molecule therapy for genetic disease / 
edited by Jess G. Thoene. 
 - xiii, 223 pages :  illustrations ;  26 cm. 
<br/><br/>Includes bibliographical references and index. 
<br/><br/><label>ISBN: </label>9780521517812  RM496.21 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Genetic Diseases, Inborn--drug therapy.<br/>Rare Diseases--drug therapy.<br/>Small Molecule Libraries--therapeutic use.<br/>Orphan Drug Production.